“Our CB-SCs can target different compartments of the immune system, educating and correcting their dysfunctions at a fundamental level,” says Dr. Zhao. “This therapy has the potential to revolutionize ...

Breakthrough Therapy designation based on clinical evidence from Phase I/II trials showing meaningful slowing of disease progression ~~ ...

Qure (QURE) announced that the U.S. Food and Drug Administration has granted Breakthrough Therapy designation to AMT-130 for the treatment ...

AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.

Shares of uniQure N.V. (NASDAQ:QURE) surged 39% following the announcement that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to AMT-130, its gene therapy ...

Qure (NASDAQ:QURE) shares added ~39% in the premarket on Thursday after the Dutch biotech announced that the FDA granted ...

At the GenScript Biotech Global Forum 2025, industry leaders celebrated CAR T cell therapy achievements while discussing ...

A multidisciplinary clinical team led by Professor Bernat Soria from the Institute of Bioengineering at the Miguel Hernández University of Elche (UMH, Spain) has developed a new method to deliver cell ...

Reducing “bad” cholesterol in the blood can stabilise changes in the vessels and cut the risk of new events, the scientists ...

Parkinson’s is a progressive neurological condition driven by the loss of dopamine-producing neurons, which causes tremors, ...

AstraZeneca and its development partner Amgen announced that the FDA has granted Breakthrough Therapy Designation (BTD) for tezepelumab in patients with severe asthma, without an eosinophilic ...

The FDA's new Breakthrough Therapy designation may offer oncology brands a powerful way forward – and some challenges for market research. Phase III in oncology – between a rock and a hard ...