Beqvez, a discontinued gene therapy for hemophilia B, reduces joint bleeding in patients, new data from Phase 3 clinical ...

Today, we're seeing more women with hemophilia diagnosed earlier, but there's still work to do, says columnist.

Columnist Allyx Formalejo says that she and her husband, Jared, are managing hemophilia in a less impulsive and more ...

Driving through the orchard, watching the leaves shimmer and fall, I came to understand something that brought me peace. Much of my life as a mother, advocate, and chaplain has been shaped by routines ...

Columnist G Shellye Horowitz applied the advocacy she learned on her hemophilia journey to get a new rare diagnosis. She ...

Every woman with a bleeding disorder knows about doubt, writes columnist. But it's important to keep speaking out.

Data from a primate study suggested MGX-001 has potential as a hemophilia A treatment, moving the drug closer to clinical ...

Hemlibra (emicizumab-kxwh) safely supports joint health in children with hemophilia A without inhibitors through three years of treatment, according to interim data from a post-marketing study in ...

Geneventiv Therapeutics said it had a “positive and constructive” meeting with the U.S. Food and Drug Administration (FDA) on its plan to develop GENV-HEM, a gene therapy for hemophilia A. The meeting ...

Biomarin Pharmaceutical is looking to sell off rights to Roctavian (valoctocogene roxaparvovec-rvox), its approved gene therapy for hemophilia A. “As we focus on the business units aligned with our ...

Doctors discovered a rare combination of blood clotting disorders — acquired hemophilia A alongside an inherited disorder called Factor XII deficiency — in a 70-year-old man set to undergo a leg ...

Men in South America with severe hemophilia A or B are hit with both direct and indirect costs related to the genetic disease, which also affect quality of life, a new study reports. As much as 99% of ...