News

Breakthrough stem cell therapy opens new treatment paths for autoimmune patients
“Our CB-SCs can target different compartments of the immune system, educating and correcting their dysfunctions at a fundamental level,” says Dr. Zhao. “This therapy has the potential to revolutionize ...
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Gene Therapy Gets Breakthrough Designation for Huntington Disease
AMT-130 is administered through magnetic resonance imaging-guided, convection-enhanced stereotactic neurosurgical delivery into the striatum.
uniQure jumps on FDA breakthrough tag for Huntington’s disease drug
Qure (NASDAQ:QURE) shares added ~39% in the premarket on Thursday after the Dutch biotech announced that the FDA granted ...
uniQure shares soar on FDA breakthrough therapy designation
Shares of uniQure N.V. (NASDAQ:QURE) surged 39% following the announcement that the U.S. Food and Drug Administration (FDA) granted Breakthrough Therapy designation to AMT-130, its gene therapy ...
uniQure Announces FDA Breakthrough Therapy Designation Granted to AMT-130 for the Treatment of Huntington’s Disease
Breakthrough Therapy designation based on clinical evidence from Phase I/II trials showing meaningful slowing of disease progression ~~ ...
uniQure granted Breakthrough Therapy Designation for AMT-130 in Huntington’s
Qure (QURE) announced that the U.S. Food and Drug Administration has granted Breakthrough Therapy designation to AMT-130 for the treatment ...