CNN

Gene therapy helps patients avoid blood transfusion, study says

"I have high hopes for the future of thalassemia," one patient says Memories of classical ballet performances dance in Wanda Sihanath’s head when she thinks about her childhood in Elgin, Illinois. She ...
Medscape

Transfusion Therapy

There is a lack of evidence-based guidelines for neonatal transfusion practices as seen by the diverse RBC transfusion practices among individuals and institutions. [3,5,27,28,29,30,31,32] The US ...
The American Journal of Managed Care

Chronic Transfusion Therapy for Sickle Cell Burdens Patients, Families, Study Says

A new study based on interviews with families and patients undergoing chronic transfusion therapy for sickle cell disease finds that the therapy affects the families in ways that extend beyond health.
The New England Journal of Medicine

Controlled Trial of Transfusions for Silent Cerebral Infarcts in Sickle Cell Anemia

Silent cerebral infarcts are the most common neurologic injury in children with sickle cell anemia and are associated with the recurrence of an infarct (stroke or silent cerebral infarct). We tested ...
News Medical

Gene therapy may be a curative treatment option for patients with transfusion-dependent beta-thalassemia

A novel gene therapy promoted transfusion independence in more than 90 percent of adult and pediatric patients with transfusion-dependent beta-thalassemia, according to a recent clinical trial ...
Medical Xpress

Gene therapy promotes transfusion independence for severe beta-thalassemia

A novel gene therapy promoted transfusion independence in more than 90 percent of adult and pediatric patients with transfusion-dependent beta-thalassemia, according to a recent clinical trial ...
Business Wire

Long-Term Data Presented at ASH Support beti-cel as a Potentially Curative Gene Therapy for β-Thalassemia Patients Who Require Regular Transfusions Through Achievement of ...

All four parent studies are complete, and all patients have transitioned to a long-term follow-up study (LTF-303) SOMERVILLE, Mass.--(BUSINESS WIRE)--Updated data from bluebird bio inc.’s (NASDAQ: ...
News Medical

Gene therapy leads to durable transfusion independence in youngest patients with thalassemia

Over 90 percent of patients with transfusion-dependent thalassemia, an inherited blood disorder, no longer needed monthly blood transfusions years after receiving gene therapy, according to an ...
Vietnam Investment Review on MSN

Base editing therapy achieves full transfusion independence in genetic blood disorders

SHANGHAI, Sept. 8, 2026 /PRNewswire/ -- On September 7, 2026, Shanghai, Cell Stem Cell published online clinical research from CorrectSequence Therapeutics (Correctseq) in collaboration with multiple ...
Medscape

Transfusion Therapy

Transfusion practices vary widely among neonatal intensive care units. The risks and benefits of transfusion as well as the disease being treated and the condition of the patient must be considered in ...
Healio

Gene therapy potentially curative for patients with transfusion-dependent beta-thalassemia

Please provide your email address to receive an email when new articles are posted on . Thompson described beta-thalassemia as a severe chronic inherited blood disorder due to one of many mutations in ...
The New England Journal of Medicine

Transfusion Therapy

THE subjects of blood and its derivatives, blood grouping, blood banking and blood transfusion were well reviewed in this journal in 1948 by Gibson 1 and in 1951 by Soutter, Allen and Emerson. 2 The ...